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Articles

February 27, 2019

U.S. FDA Grants Breakthrough Therapy Designation to Amicus Therapeutics February 27, 2019

Amicus Therapeutics recently announced that the US FDA has granted to Amicus a Breakthrough Therapy Designation (BTD) to AT-GAA for the treatment of late onset Pompe disease, an inherited lysosomal storage disorder caused by the deficiency of an enzyme known as acid alpha-glucosidase (GAA).

November 20, 2017

CANCER IMMUNOTHERAPY - Building on Initial Successes to Improve Clinical Outcomes November 20, 2017

Allan B. Haberman, PhD, provides an updated discussion of approved and clinical-stage agents in immuno-oncology, including recently approved agents. He also addresses how researchers and companies are attempting to build on prior achievements in immuno-oncology to improve outcomes for more patients.

November 7, 2016

PLATFORM TECHNOLOGY - ​​The 3DNA® Platform for Targeted Drug Delivery November 7, 2016

Robert C. Getts, PhD, and Jessica Bowers review how the 3DNA platform is composed entirely of noncoding DNA assembled through the sequential hybridization of single strands of DNA into a network of double-stranded nucleic acid having a controlled architecture, and multiple attachment sites for drug and targeting molecules.

September 27, 2011

10/4/2011 September 27, 2011

Talon Therapeutics' NDA Accepted for Filing by US FDA Under Subpart H Talon Therapeutics, Inc. recently announced its NDA seeking...
May 19, 2011

5/24/2011 May 19, 2011

Sartorius Stedim Biotech & RAUMEDIC Sign Partnership Agreement Sartorius Stedim Biotech (SSB), an international leading pharma and biotech supplier, and...